Have you or your loved ones been diagnosed with adrenoleukodystrophy?

You may be eligible to participate in a adrenoleukodystrophy clinical trial.

Have you or your loved ones been diagnosed with adrenoleukodystrophy? You may be eligible to participate in a adrenoleukodystrophy clinical trial.

What is a clinical trial? Is participating in a clinical trial right for you? Learn more

Recruiting for this study? Get access to patient recruitment tools.
Adrenoleukodystrophy Clinical Trial in Durham NC
NCT02254863 | Phase 1 | Interventional
Joanne Kurtzberg MD
Sponsored by
Joanne Kurtzberg MD

Have you or your loved ones been diagnosed with adrenoleukodystrophy?

You may be eligible to participate in a adrenoleukodystrophy clinical trial.

Have you or your loved ones been diagnosed with adrenoleukodystrophy? You may be eligible to participate in a adrenoleukodystrophy clinical trial.

Recruiting

Male & Female

Up to 22

Years old

This study is looking to recruit 12 Participants

The primary objective of the study is to determine the safety and feasibility of intrathecal administration of DUOC-01 as an adjunctive therapy in patients with inborn errors of metabolism who have evidence of early demyelinating disease in the central nervous system (CNS) who are undergoing standard treatment with unrelated umbilical cord blood transplantation (UCBT). The secondary objective of the study is to describe the efficacy of UCBT with intrathecal administration of DUOC-01 in these patients.

Where you'll go

Selected location

Duke University Medical Center

Duke University Medical Center Change

1400 Morreene Road, Durham, NC, USA 27705
Map | Learn more
Step 1 of 4: Email
Selected location

Duke University Medical Center

1400 Morreene Road, Durham, NC, USA 27705


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